Lebers congential amaurosis gene therapy (University Medical Center St Radboud)

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Report date: 2025/02/01 20:00:06

Base Information

Drug NameLebers congential amaurosis gene therapy (University Medical Center St Radboud)
Drug Alias NameN/A
ClassificationBiologics
Mechanisms of ActionCentrosomal protein of 290 kDa modulators
TargetsCentrosomal protein of 290 kDa
Therapy Area/IndicationsLeber Congenital Amaurosis
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryNetherlands
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Active IndicationsN/A
Inactive IndicationsLeber Congenital Amaurosis

Other Information

ATC CodeN/A
Related LinksN/A