AAV gene therapy (Sarepta/Columbia University)

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Report date: 2025/01/26 18:05:12

Base Information

Drug NameAAV gene therapy (Sarepta/Columbia University)
Drug Alias NameAAV gene therapy (Sarepta/StrideBio)
ClassificationBiologics
Mechanisms of ActionMusculoskeletal system modulators
TargetsUpdating
Therapy Area/IndicationsMuscular Dystrophy, Emery-Dreifuss
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesSarepta Therapeutics Inc
China Registration ClassN/A

Develop Information

Inactive CompaniesStridebio Inc
Active IndicationsMuscular Dystrophy, Emery-Dreifuss
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A