AAV.SAN002-hARSA

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Report date: 2025/01/26 18:05:17

Base Information

Drug NameAAV.SAN002-hARSA
Drug Alias NameAAV-mediated ARSA gene replacement therapy (Sanofi)
ClassificationBiologics
Mechanisms of ActionARSA gene transference
TargetsCerebroside-sulfatase
Therapy Area/IndicationsLeukodystrophy, Metachromatic
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesSanofi
China Registration ClassN/A

Develop Information

Active CompaniesSanofi
Inactive CompaniesN/A
Active IndicationsLeukodystrophy, Metachromatic
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A