AAV8-AAT-ATP7B

N/A

Report date: 2025/01/26 18:11:23

Base Information

Drug NameAAV8-AAT-ATP7B
Drug Alias NameAAV8 ATP7B gene therapy (Aligen Therapeutics)AAV8-AAT-ATP7B
ClassificationBiologics
Mechanisms of ActionCopper-transporting ATPase 2 gene transference
TargetsCopper-transporting ATPase 2
Therapy Area/IndicationsHepatolenticular Degeneration
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritorySpain
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesUniversity Of Navarra
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsHepatolenticular Degeneration
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A