AAV9 vector-based miR-132 therapy (Japan National Institute of Neuroscience)

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Report date: 2025/01/26 15:58:21

Base Information

Drug NameAAV9 vector-based miR-132 therapy (Japan National Institute of Neuroscience)
Drug Alias NameAAV8 gene therapy (Gordian Biotechnology)adeno-associated virus (AAV) serotype rh.10 vector carrying NPC2 HA peptide (Weill Medical College of Cornell University)gene therapy (Gordian Biotechnology)huntingtin gene-targeted AAV-microRNA (Genzyme)
ClassificationBiologics
Mechanisms of ActionFibroblast growth factor 19 stimulants
TargetsFibroblast growth factor 19
Therapy Area/IndicationsMetabolic Dysfunction-Associated Steatotic Liver Disease
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesGordian Biotechnology Inc
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsMetabolic Dysfunction-Associated Steatotic Liver Disease
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A