AAV9 vector-based AP4B1 gene therapy (Cure AP-4)

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Report date: 2025/01/26 18:11:25

Base Information

Drug NameAAV9 vector-based AP4B1 gene therapy (Cure AP-4)
Drug Alias Nameadeno-associated virus serotype 9 gene transfer vector expressing human AP4B1 cDNA (Cure AP-4)
ClassificationBiologics
Mechanisms of ActionAP-4 complex subunit mu-1 modulators
TargetsAP-4 complex subunit mu-1
Therapy Area/IndicationsSpastic Paraplegia, Hereditary
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesCure AP-4 Foundation
China Registration ClassN/A

Develop Information

Active CompaniesCure AP-4 Foundation
Inactive CompaniesN/A
Active IndicationsSpastic Paraplegia, Hereditary
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A