AAV9-based gene replacement therapy (University of Texas Southwestern Medical Center)

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Report date: 2025/02/01 20:00:06

Base Information

Drug NameAAV9-based gene replacement therapy (University of Texas Southwestern Medical Center)
Drug Alias NameMFSD8 gene therapy (University of Texas Southwestern Medical Center)
ClassificationBiologics
Mechanisms of ActionUpdating
TargetsUpdating
Therapy Area/IndicationsLysosomal Storage Diseases
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPhase 1 Clinical
Highest Status in ChinaN/A
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsLysosomal Storage Diseases
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A