AAV-ATP7A

N/A

Report date: 2026/02/28 12:01:23

Base Information

Drug NameAAV-ATP7A
Drug Alias NameAAV-based ATP7A gene therapy (Cyprium Therapeutics/NICHD)AAV5-rsATP7A cDNA (NIH)rAAV9-rsATP7ArsATP7A cDNAATP7A gene therapy (NIH) +[6] 
ClassificationBiologics
Mechanisms of ActionATP7A gene transference
TargetsCopper-transporting ATPase 1
Therapy Area/IndicationsMenkes Kinky Hair Syndrome
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesEunice Kennedy Shriver Institute Of Child Health And Human Development
China Registration ClassN/A

Develop Information

Active CompaniesEunice Kennedy Shriver Institute Of Child Health And Human DevelopmentCyprium Therapeutics Inc
Inactive CompaniesN/A
Active IndicationsMenkes Kinky Hair Syndrome
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A