AAVB1-GAA

N/A

Report date: 2025/01/26 15:58:23

Base Information

Drug NameAAVB1-GAA
Drug Alias Nameadeno-associated caspid virus alpha-glucosidase gene therapy (University of Massachussets Medical School)AAVB1-GAA
ClassificationBiologics
Mechanisms of ActionAcidic alpha-glucosidase modulators
TargetsAcidic alpha-glucosidase
Therapy Area/IndicationsGlycogen Storage Disease Type II
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsGlycogen Storage Disease Type II
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A