AAV-GBA1

N/A

Report date: 2025/01/26 18:17:47

Base Information

Drug NameAAV-GBA1
Drug Alias NameAAV-based GBA1 gene therapy (Biogen)GBA1 gene therapy (Biogen)AAV-based gene therapy (Biogen)AAV-GBA1
ClassificationBiologics
Mechanisms of ActionBeta-glucocerebrosidase stimulants
TargetsBeta-glucocerebrosidase
Therapy Area/IndicationsParkinson Disease
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesBiogen Inc
China Registration ClassN/A

Develop Information

Active CompaniesBiogen Inc
Inactive CompaniesN/A
Active IndicationsParkinson Disease
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A