AAV-SMN1

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Report date: 2025/01/26 18:17:52

Base Information

Drug NameAAV-SMN1
Drug Alias Nameadeno-associated virus based SMN1 gene therapy (Intas)AAV-SMN1
ClassificationBiologics
Mechanisms of ActionSurvival motor neuron protein stimulants
TargetsSurvival motor neuron protein
Therapy Area/IndicationsMuscular Atrophy, Spinal
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryIndia
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesIntas Pharmaceuticals Ltd
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsMuscular Atrophy, Spinal
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A