ABCA4 gene therapy (Beacon Therapeutics Holdings)

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Report date: 2025/01/26 18:18:06

Base Information

Drug NameABCA4 gene therapy (Beacon Therapeutics Holdings)
Drug Alias NameABCA4 gene therapy (Applied Genetic technologies)
ClassificationBiologics
Mechanisms of ActionRetinal-specific phospholipid-transporting ATPase ABCA4 stimulants
TargetsRetinal-specific phospholipid-transporting ATPase ABCA4
Therapy Area/IndicationsStargardt Disease
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesBeacon Therapeutics Holdings Ltd
China Registration ClassN/A

Develop Information

Active CompaniesBeacon Therapeutics Holdings Ltd
Inactive CompaniesN/A
Active IndicationsStargardt Disease
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A