adeno-associated virus vector based gene therapy (Adverum/Editas Medicine)

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Report date: 2025/01/26 18:50:04

Base Information

Drug Nameadeno-associated virus vector based gene therapy (Adverum/Editas Medicine)
Drug Alias NameGC1 gene editing therapy (Editas Medicine)
ClassificationBiologics
Mechanisms of ActionRetinal guanylyl cyclase 1 modulators
TargetsRetinal guanylyl cyclase 1
Therapy Area/IndicationsRetinal DiseasesRetinal Dysplasia
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesAdverum Biotechnologies Inc
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsRetinal DiseasesRetinal Dysplasia
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A