MALAT1 stereopure antisense oligonucleotide therapy (Wave Life Sciences)

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Report date: 2025/02/01 20:00:06
NME

Base Information

Drug NameMALAT1 stereopure antisense oligonucleotide therapy (Wave Life Sciences)
Drug Alias Namerare genetic eye diseases program 1 (WaVe Life Sciences)
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionMetastasis Associated Lung Adenocarcinoma Transcript 1 inhibitors
TargetsMetastasis Associated Lung Adenocarcinoma Transcript 1
Therapy Area/IndicationsGenetic Diseases, InbornEye Diseases
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited StatesJapan
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesWave Life Sciences Ltd
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesWave Life Sciences Ltd
Active IndicationsN/A
Inactive IndicationsGenetic Diseases, InbornEye Diseases

Other Information

ATC CodeN/A
Related LinksN/A