ION-648402

N/A

Report date: 2025/01/26 19:21:52
NME

Base Information

Drug NameION-648402
Drug Alias NameLafora disease therapy (Ionis Pharma)ION-648402
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionGlycogen synthase 1 inhibitors
TargetsGlycogen synthase 1
Therapy Area/IndicationsLafora Disease
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesIonis Pharmaceuticals Inc
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsLafora Disease
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A