lentiviral vector based gene therapy (Genespire/San Raffaele Telethon Institute)

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Report date: 2025/01/26 19:10:22

Base Information

Drug Namelentiviral vector based gene therapy (Genespire/San Raffaele Telethon Institute)
Drug Alias Namein-vivo gene therapy (Genespire/San Raffaele Telethon Institute)
ClassificationBiologics
Mechanisms of ActionMethylmalonyl-CoA Mutase gene transference
TargetsMethylmalonyl-CoA Mutase
Therapy Area/IndicationsMethylmalonic acidaemiaLiver Diseases
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryItaly
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesGenespire SRL
China Registration ClassN/A

Develop Information

Active CompaniesGenespire SRLThe San Raffaele Telethon Institute For Gene Therapy
Inactive CompaniesN/A
Active IndicationsMethylmalonic acidaemiaLiver Diseases
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A