SPK-10000

N/A

Report date: 2025/01/26 18:13:01

Base Information

Drug NameSPK-10000
Drug Alias NameSERPING1 gene therapy (Spark Therapeutics)adeno-associated virus vector based gene therapy (Spark Therapeutics)SPK-10000
ClassificationBiologics
Mechanisms of ActionPlasma protease C1 inhibitor gene transference
TargetsPlasma protease C1 inhibitor
Therapy Area/IndicationsAngioedemas, Hereditary
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesSpark Therapeutics Inc
China Registration ClassN/A

Develop Information

Active CompaniesSpark Therapeutics Inc
Inactive CompaniesN/A
Active IndicationsAngioedemas, Hereditary
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A