myotubularin gene-encoding AAV 8 vector based therapy (Genethon/Wake Forest University/University of Washington/Harvard Medical School/INSERM)

N/A

Report date: 2025/01/26 18:25:45

Base Information

Drug Namemyotubularin gene-encoding AAV 8 vector based therapy (Genethon/Wake Forest University/University of Washington/Harvard Medical School/INSERM)
Drug Alias Namemyotubularin gene-containing AAV vector based therapy (Genethon/Wake Forest University)AAV-MTM1
ClassificationBiologics
Mechanisms of ActionMyotubularin modulators
TargetsMyotubularin
Therapy Area/IndicationsMyopathies, Structural, Congenital
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited StatesFrance
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesGenethon
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsMyopathies, Structural, Congenital
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A