MYR-103

N/A

Report date: 2025/01/26 17:29:52
NME

Base Information

Drug NameMYR-103
Drug Alias NamePlp1 gene therapy (Myrtelle)MYR-103
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > microRNA
Mechanisms of ActionMyelin proteolipid protein inhibitors
TargetsMyelin proteolipid protein
Therapy Area/IndicationsPelizaeus-Merzbacher Disease
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesMyrtelle Inc
China Registration ClassN/A

Develop Information

Active CompaniesMyrtelle Inc
Inactive CompaniesN/A
Active IndicationsPelizaeus-Merzbacher Disease
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A