lentiviral vector-transduced stem cell gene therapy (Fondazione Telethon)

N/A

Report date: 2025/01/26 18:25:53

Base Information

Drug Namelentiviral vector-transduced stem cell gene therapy (Fondazione Telethon)
Drug Alias NameN-acetylgalactosamine-6-sulfatase stimulator (Fondazione Telethon)
ClassificationCell and gene therapy > Cell therapy > Stem cell therapy > Hematopoietic stem cells therapy
Mechanisms of ActionHematopoietic progenitor cell antigen CD34 modulatorsN-acetylgalactosamine-6-sulfatase stimulants
TargetsHematopoietic progenitor cell antigen CD34N-acetylgalactosamine-6-sulfatase
Therapy Area/IndicationsMucopolysaccharidosis IV
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryEurope
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesFondazione Telethon
China Registration ClassN/A

Develop Information

Active CompaniesFondazione Telethon
Inactive CompaniesN/A
Active IndicationsMucopolysaccharidosis IV
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A