QRX-333

N/A

Report date: 2025/02/25 13:37:53
NME

Base Information

Drug NameQRX-333
Drug Alias NameCOL7A1 antisense oligonucleotide exon skipping therapy (ProQR Therapeutics)COL7A1 antisense oligonucleotide exon skipping therapy (Wing Therapeutics)QRX-333
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionCOL7A1 gene transference
TargetsCollagen alpha-1(VII) chainRibonucleic Acid
Therapy Area/IndicationsEpidermolysis Bullosa Dystrophica
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited StatesNetherlands
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesProqr Therapeutics Nv
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesProqr Therapeutics NvWings Therapeutics Inc
Active IndicationsN/A
Inactive IndicationsEpidermolysis Bullosa Dystrophica

Other Information

ATC CodeN/A
Related LinksN/A