RNA actuator therapeutic for urea cycle disorder(CAMP4 Therapeutics)

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Report date: 2025/01/26 16:56:45
NME

Base Information

Drug NameRNA actuator therapeutic for urea cycle disorder(CAMP4 Therapeutics)
Drug Alias Nameantisense oligonucleotide for urea cycle disorder(CAMP4 Therapeutics)
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionOrnithine carbamoyltransferase stimulants
TargetsOrnithine carbamoyltransferase
Therapy Area/IndicationsUrea Cycle Disorders, Inborn
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesCamp4 Therapeutics Corp
China Registration ClassN/A

Develop Information

Active CompaniesCamp4 Therapeutics Corp
Inactive CompaniesN/A
Active IndicationsUrea Cycle Disorders, Inborn
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A