quasidystrophin gene therapy (Genethon/INSERM UMR S951)

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Report date: 2025/01/26 16:50:55

Base Information

Drug Namequasidystrophin gene therapy (Genethon/INSERM UMR S951)
Drug Alias NameN/A
ClassificationBiologics
Mechanisms of ActionDystrophin modulators
TargetsDystrophin
Therapy Area/IndicationsMuscular Dystrophy, Duchenne
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryFrance
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesGenethon
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsMuscular Dystrophy, Duchenne
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A