RNA-inhibiting small molecules for genetic disorders(Arrakis Therapeutics)

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Report date: 2025/01/26 17:03:42
NME

Base Information

Drug NameRNA-inhibiting small molecules for genetic disorders(Arrakis Therapeutics)
Drug Alias NameRNA-targeted small molecules for genetic disorders(Arrakis Therapeutics)
ClassificationSmall molecules > Heterocyclic drugs
Mechanisms of ActionRNA modulators
TargetsRibonucleic Acid
Therapy Area/IndicationsGenetic Diseases, Inborn
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesArrakis Therapeutics Inc
China Registration ClassN/A

Develop Information

Active CompaniesArrakis Therapeutics Inc
Inactive CompaniesN/A
Active IndicationsGenetic Diseases, Inborn
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A