next generation mRNA therapy (Translate Bio)

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Report date: 2025/05/14 13:52:04

Base Information

Drug Namenext generation mRNA therapy (Translate Bio)
Drug Alias NamemRNA therapy for cystic fibrosis(Translate Bio)
ClassificationCell and gene therapy > Gene therapy > mRNASmall molecules > Nucleosides and nucleotide derivtives > OligonucleotideSmall molecules > Lipid
Mechanisms of ActionCystic fibrosis transmembrane conductance regulator modulators
TargetsCystic fibrosis transmembrane conductance regulator
Therapy Area/IndicationsCystic Fibrosis
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesTranslate Bio Ma Inc
China Registration ClassN/A

Develop Information

Active CompaniesTranslate Bio Ma Inc
Inactive CompaniesN/A
Active IndicationsCystic Fibrosis
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A