SMN1 gene modulator (X-linked infantile spinal muscular atrophy) (Recursion)

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Report date: 2025/02/01 20:00:06
NME

Base Information

Drug NameSMN1 gene modulator (X-linked infantile spinal muscular atrophy) (Recursion)
Drug Alias Namerepurposed therapeutics (X-linked infantile spinal muscular atrophy) (Recursion)survival motor neuron-1 gene modulator (X-linked infantile spinal muscular atrophy) (Recursion)
ClassificationSmall molecules > Heterocyclic drugs
Mechanisms of ActionSurvival motor neuron protein modulators
TargetsSurvival motor neuron protein
Therapy Area/IndicationsMuscular Atrophy, Spinal
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesRecursion Pharmaceuticals Inc
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Active IndicationsN/A
Inactive IndicationsMuscular Atrophy, Spinal

Other Information

ATC CodeN/A
Related LinksN/A