sodium phenylbutyrate (GMP-Orphan)

N/A

Report date: 2025/02/01 20:00:06
NME

Base Information

Drug Namesodium phenylbutyrate (GMP-Orphan)
Drug Alias Namesodium 4-phenylbutyrateGMA-101
ClassificationSmall molecules > Heterocyclic drugs
Mechanisms of ActionHistone deacetylase inhibitors
TargetsHistone deacetylase
Therapy Area/IndicationsMuscular Atrophy, Spinal
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited StatesFrance
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesGmp-Orphan Sas
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesGmp-Orphan Sas
Active IndicationsN/A
Inactive IndicationsMuscular Atrophy, Spinal

Other Information

ATC CodeN/A
Related LinksN/A