VY-NPC-101

N/A

Report date: 2025/01/26 15:11:08

Base Information

Drug NameVY-NPC-101

Drug Alias NameNPC1 gene therapy (AAV) (Voyager)NPC1 gene therapy (adeno-associated viral vector) (Voyager)AAV-based gene therapy (Voyager Therapeutics)VY-NPC-101

ClassificationBiologics

Mechanisms of ActionNPC Intracellular Cholesterol Transporter 1 inhibitors

TargetsNPC Intracellular Cholesterol Transporter 1

Therapy Area/IndicationsNiemann-Pick Disease, Type C

Global Approved IndicationsN/A

Approved Indications in ChinaN/A

Original Approved Country/TerritoryN/A

Original Approved DateN/A

Country/TerritoryUnited States

CombinationsNo

Global Highest StatusPreclinical

Highest Status in ChinaN/A

Originator CompaniesVoyager Therapeutics Inc

China Registration ClassN/A

Develop Information

Active CompaniesVoyager Therapeutics Inc

Inactive CompaniesN/A

Active IndicationsNiemann-Pick Disease, Type C

Inactive IndicationsN/A

Other Information

ATC CodeN/A