VY-SMN-101

N/A

Report date: 2025/02/01 20:00:06

Base Information

Drug NameVY-SMN-101
Drug Alias NameAAV-based gene therapy (Voyager Therapeutics)AAV-based gene therapy (Voyager Therapeutics/Genzyme)VY-SMN-101
ClassificationBiologics
Mechanisms of ActionSurvival motor neuron protein inhibitors
TargetsSurvival motor neuron protein
Therapy Area/IndicationsMuscular Atrophy, Spinal
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusDiscontinued (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesVoyager Therapeutics Inc
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesVoyager Therapeutics Inc
Active IndicationsN/A
Inactive IndicationsMuscular Atrophy, Spinal

Other Information

ATC CodeN/A
Related LinksN/A