WVE-3972-01

N/A

Report date: 2025/01/26 15:44:35
NME

Base Information

Drug NameWVE-3972-01
Drug Alias NameC9orf72 targeting program (WaVe Life Sciences)WVE-3972-01
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionGuanine nucleotide exchange C9orf72 modulators
TargetsGuanine nucleotide exchange C9orf72
Therapy Area/IndicationsAmyotrophic Lateral SclerosisFrontotemporal Dementia
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritorySingapore
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesWave Life Sciences Ltd
China Registration ClassN/A

Develop Information

Active CompaniesWave Life Sciences Ltd
Inactive CompaniesN/A
Active IndicationsAmyotrophic Lateral SclerosisFrontotemporal Dementia
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A