UBE3A gene therapy (PTC Therapeutics)

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Report date: 2025/01/26 16:35:35

Base Information

Drug NameUBE3A gene therapy (PTC Therapeutics)
Drug Alias NameAAV9-UBE3A gene therapy (PTC Therapeutics)
ClassificationBiologics
Mechanisms of ActionUbiquitin-like modifier-activating enzyme 3A stimulants
TargetsUbiquitin-like modifier-activating enzyme 3A
Therapy Area/IndicationsAngelman Syndrome
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryEurope
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesPtc Therapeutics Inc
China Registration ClassN/A

Develop Information

Active CompaniesPtc Therapeutics Inc
Inactive CompaniesN/A
Active IndicationsAngelman Syndrome
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A