adeno-associated viral vector-based gene therapy (Real Regulatory)

N/A

Report date: 2025/03/14 16:27:12

Base Information

Drug Nameadeno-associated viral vector-based gene therapy (Real Regulatory)

Drug Alias NameCLNS gene modulator (Real Regulatory)adeno-associated virus serotype 9 expressing human CLN5 (Real Regulatory)adeno-associated virus serotype 9 vector-delivered CLNS gene therapy (Real Regulatory)

ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector

Mechanisms of ActionCLN5 Intracellular Trafficking Protein modulators

TargetsCLN5 Intracellular Trafficking Protein

Therapy Area/IndicationsNeuronal Ceroid-Lipofuscinoses

Global Approved IndicationsN/A

Approved Indications in ChinaN/A

Original Approved Country/TerritoryN/A

Original Approved DateN/A

Country/TerritoryIreland

CombinationsNo

Global Highest StatusPreclinical

Highest Status in ChinaN/A

Originator CompaniesReal Regulatory Ltd

China Registration ClassN/A

Develop Information

Active CompaniesReal Regulatory Ltd

Inactive CompaniesN/A

Active IndicationsNeuronal Ceroid-Lipofuscinoses

Inactive IndicationsN/A

Other Information

ATC CodeN/A