adeno-associated virus vector gene therapy (Genethon)

N/A

Report date: 2025/03/14 20:00:48

Base Information

Drug Nameadeno-associated virus vector gene therapy (Genethon)

Drug Alias NameN/A

ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector

Mechanisms of ActionNeuroprotectants

TargetsUpdating

Therapy Area/IndicationsMucopolysaccharidosis III

Global Approved IndicationsN/A

Approved Indications in ChinaN/A

Original Approved Country/TerritoryN/A

Original Approved DateN/A

Country/TerritoryFrance

CombinationsNo

Global Highest StatusPending (Preclinical)

Highest Status in ChinaN/A

Originator CompaniesGénéthon

China Registration ClassN/A

Active CompaniesN/A

Inactive CompaniesGénéthon

Active IndicationsN/A

Inactive IndicationsMucopolysaccharidosis III

ATC CodeN/A