AAV8-delivered APOC3-specific meganuclease (Precision BioSciences/University of Pennsylvania)

N/A

Report date: 2025/03/14 16:43:43

Base Information

Drug NameAAV8-delivered APOC3-specific meganuclease (Precision BioSciences/University of Pennsylvania)
Drug Alias NameAPOC3-specific meganuclease (Precision BioSciences/University of Pennsylvania)
ClassificationBiologics > Protein drugs > Enzyme > Recombinant enzymeBiologics > Protein drugs > Recombinant protein > Recombinant enzymeCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionApolipoprotein C-III inhibitors
TargetsApolipoprotein C-III
Therapy Area/IndicationsHyperlipoproteinemia Type I
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesPrecision Biosciences Inc
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsHyperlipoproteinemia Type I
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A