AAV8-delivered TTR-specific ARCUS meganuclease (Precision BioSciences)

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Report date: 2025/03/14 20:00:48

Base Information

Drug NameAAV8-delivered TTR-specific ARCUS meganuclease (Precision BioSciences)
Drug Alias NameTTR-specific meganuclease (Precision BioSciences)
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vectorBiologics > Protein drugs > Enzyme > Recombinant enzymeBiologics > Protein drugs > Recombinant protein > Recombinant enzyme
Mechanisms of ActionTransthyretin inhibitors
TargetsTransthyretin
Therapy Area/IndicationsPolyneuropathies
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesPrecision Biosciences Inc
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesPrecision Biosciences Inc
Active IndicationsN/A
Inactive IndicationsPolyneuropathies

Other Information

ATC CodeN/A
Related LinksN/A