AAV8-GPE gene therapy (NICHD)

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Report date: 2025/03/14 20:00:48

Base Information

Drug NameAAV8-GPE gene therapy (NICHD)
Drug Alias NameN/A
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionGlucose-6-phosphatase stimulants
TargetsGlucose-6-phosphatase
Therapy Area/IndicationsGlycogen Storage Disease Type I
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesEunice Kennedy Shriver Institute Of Child Health And Human Development
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesEunice Kennedy Shriver Institute Of Child Health And Human Development
Active IndicationsN/A
Inactive IndicationsGlycogen Storage Disease Type I

Other Information

ATC CodeN/A
Related LinksN/A