AAV9-NK1-shRNA (Ionis Pharmaceuticals/University of California)

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Report date: 2025/03/14 20:00:48

Base Information

Drug NameAAV9-NK1-shRNA (Ionis Pharmaceuticals/University of California)
Drug Alias NameAAV9-NK1-shRNA
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionNeurokinin 1 receptor antagonists
TargetsNeurokinin 1 receptor
Therapy Area/IndicationsMuscle Hypertonia
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesIonis Pharmaceuticals Inc
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Active IndicationsN/A
Inactive IndicationsMuscle Hypertonia

Other Information

ATC CodeN/A
Related LinksN/A