alpha-L-iduronidase-apolipoprotein E fusion proteins (Cincinnati Children's Hospital Medical Center)

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Report date: 2025/03/14 20:00:48

Base Information

Drug Namealpha-L-iduronidase-apolipoprotein E fusion proteins (Cincinnati Children's Hospital Medical Center)
Drug Alias NameIDUA-apoE fusion proteins (Cincinnati Children's Hospital Medical Center)IDUAe1IDUAe2
ClassificationBiologics > Protein drugs > Recombinant protein > Fusion proteinBiologics > Protein drugs > Enzyme > Recombinant enzymeBiologics > Protein drugs > Recombinant protein > Recombinant enzyme
Mechanisms of ActionAlpha-L-iduronidase stimulantsLDL receptor modulatorsGlycosaminoglycan modulators +[4
TargetsGlycosaminoglycanAlpha-L-iduronidaseLDL receptor +[4
Therapy Area/IndicationsMucopolysaccharidosis I
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Active IndicationsN/A
Inactive IndicationsMucopolysaccharidosis I

Other Information

ATC CodeN/A
Related LinksN/A