allosteric GALC regulator program (Gain Therapeutics)

N/A

Report date: 2025/03/14 16:30:32
NME

Base Information

Drug Nameallosteric GALC regulator program (Gain Therapeutics)
Drug Alias NameGALC gene stimulator (Gain Therapeutics)
ClassificationSmall molecules > Heterocyclic drugs
Mechanisms of ActionGalactocerebrosidase stimulants
TargetsGalactocerebrosidase
Therapy Area/IndicationsLeukodystrophy, Globoid Cell
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesGain Therapeutics Inc
China Registration ClassN/A

Develop Information

Active CompaniesGain Therapeutics Inc
Inactive CompaniesN/A
Active IndicationsLeukodystrophy, Globoid Cell
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A