antisense oligonucleotide (Cold spring harbor laboratory/Ionis Pharmaceuticals)

N/A

Report date: 2025/03/14 20:00:48
NME

Base Information

Drug Nameantisense oligonucleotide (Cold spring harbor laboratory/Ionis Pharmaceuticals)
Drug Alias NameASO 7-26S (PS-MOE)
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionElongator complex protein 1 modulators
TargetsElongator complex protein 1
Therapy Area/IndicationsDysautonomia, Familial
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesCold Spring Harbor Laboratory
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Active IndicationsN/A
Inactive IndicationsDysautonomia, Familial

Other Information

ATC CodeN/A
Related LinksN/A