antisense oligonucleotides (Genzyme/Isis Pharmaceuticals)

N/A

Report date: 2025/03/14 20:00:48
NME

Base Information

Drug Nameantisense oligonucleotides (Genzyme/Isis Pharmaceuticals)
Drug Alias Name2-MOE phosphorothioate gapmers (Genzyme/Isis Pharmaceuticals)oligo445236oligo445238
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionMyotonin-protein kinase inhibitors
TargetsMyotonin-protein kinase
Therapy Area/IndicationsMyotonic Dystrophy
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesGenzyme Corp
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Active IndicationsN/A
Inactive IndicationsMyotonic Dystrophy

Other Information

ATC CodeN/A
Related LinksN/A