autologous HSC cells transduced with a lentiviral vector-delivered IDUA modified gene (bluebird bio/University of Minnesota)

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Report date: 2025/03/14 16:32:40

Base Information

Drug Nameautologous HSC cells transduced with a lentiviral vector-delivered IDUA modified gene (bluebird bio/University of Minnesota)
Drug Alias NameIDUA gene therapy (bluebird bio/University of Minnesota)
ClassificationCell and gene therapy > Cell therapy > Stem cell therapy > Hematopoietic stem cells therapy
Mechanisms of ActionAlpha-L-iduronidase stimulants
TargetsAlpha-L-iduronidase
Therapy Area/Indications +[1]  N/A
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesUniversity Of Minnesota
China Registration ClassN/A

Develop Information

Active CompaniesUniversity Of MinnesotaGenetix Biotherapeutics Inc
Inactive CompaniesN/A
Active Indications +[1]  N/A
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A