beta globin-specific ribozyme (Ribozyme)

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Report date: 2025/03/14 20:00:48
NME

Base Information

Drug Namebeta globin-specific ribozyme (Ribozyme)
Drug Alias NameN/A
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Ribozyme
Mechanisms of ActionHemoglobin beta chain modulators
TargetsHemoglobin beta chain
Therapy Area/IndicationsAnemia, Sickle Cell
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesDuke University
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Active IndicationsN/A
Inactive IndicationsAnemia, Sickle Cell

Other Information

ATC CodeN/A
Related LinksN/A