Canavan disease therapeutics (Orphan Star Therapeutics)

N/A

Report date: 2025/03/14 16:34:17
NME

Base Information

Drug NameCanavan disease therapeutics (Orphan Star Therapeutics)
Drug Alias NameASPA gene modulator (Orphan Star Therapeutics)
ClassificationSmall molecules > Heterocyclic drugs
Mechanisms of ActionASPA gene modulators
TargetsAspartoacylase
Therapy Area/IndicationsCanavan Disease
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesOrphan Star Therapeutics Llc
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsCanavan Disease
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A