CFTR gene therapy (Arbor/Vertex)

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Report date: 2025/03/18 18:08:40

Base Information

Drug NameCFTR gene therapy (Arbor/Vertex)
Drug Alias Namegene-editing therapies (Arbor/Vertex)
ClassificationCell and gene therapy > Gene therapy
Mechanisms of ActionCystic fibrosis transmembrane conductance regulator modulators
TargetsCystic fibrosis transmembrane conductance regulator
Therapy Area/IndicationsCystic Fibrosis
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesArbor Biotechnologies Inc
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsCystic Fibrosis
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A