ex vivo MNDU3-IDS-tranduced hematopoietic stem cell therapy (bluebird bio/University of Minnesota)

N/A

Report date: 2025/03/20 15:49:01

Base Information

Drug Nameex vivo MNDU3-IDS-tranduced hematopoietic stem cell therapy (bluebird bio/University of Minnesota)
Drug Alias NameMNDU3-IDS transduced HSCs (bluebird bio/University of Minnesota)MNDU3-IDS lenti viral therapy (bluebird bio/University of Minnesota)
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Lentiviral vectorCell and gene therapy > Cell therapy > Stem cell therapy > Hematopoietic stem cells therapy
Mechanisms of ActionIduronate-2-sulfatase gene transference
TargetsIduronate-2-sulfatase
Therapy Area/IndicationsMucopolysaccharidosis II
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesGenetix Biotherapeutics Inc
China Registration ClassN/A

Develop Information

Active CompaniesUniversity Of MinnesotaGenetix Biotherapeutics Inc
Inactive CompaniesN/A
Active IndicationsMucopolysaccharidosis II
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A