encapsulated non-viral cell-based therapy secreting ARSB (Sigilon Therapeutics)

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Report date: 2025/03/20 20:00:06

Base Information

Drug Nameencapsulated non-viral cell-based therapy secreting ARSB (Sigilon Therapeutics)
Drug Alias Nameencapsulated allogeneic human cells secreting arylsulfatase B (Sigilon Therapeutics)
ClassificationCell and gene therapy > Cell therapyBiologics > Protein drugs > Enzyme > Recombinant enzymeBiologics > Protein drugs > Recombinant protein > Recombinant enzyme
Mechanisms of ActionArylsulfatase B stimulants
TargetsArylsulfatase B
Therapy Area/IndicationsMucopolysaccharidosis VI
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesSigilon Therapeutics Inc
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesSigilon Therapeutics Inc
Active IndicationsN/A
Inactive IndicationsMucopolysaccharidosis VI

Other Information

ATC CodeN/A
Related LinksN/A