gene splicing modulator (PTC Therapeutics)

N/A

Report date: 2025/03/20 15:54:33
NME

Base Information

Drug Namegene splicing modulator (PTC Therapeutics)
Drug Alias NameN/A
ClassificationSmall molecules > Heterocyclic drugs
Mechanisms of ActionAtaxin-3 modulators
TargetsAtaxin-3
Therapy Area/IndicationsMachado-Joseph Disease
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesPtc Therapeutics Inc
China Registration ClassN/A

Develop Information

Active CompaniesPtc Therapeutics Inc
Inactive CompaniesN/A
Active IndicationsMachado-Joseph Disease
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A