CFTR gene therapy (UCSF/Uni South Carolina)

N/A

Report date: 2025/03/20 20:00:06

Base Information

Drug NameCFTR gene therapy (UCSF/Uni South Carolina)
Drug Alias Nametruncated CFTR gene therapy (UCSF/Univ South Carolina)CFTR mini-genes (UCSF/Univ South Carolina)
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionUpdating
TargetsUpdating
Therapy Area/IndicationsCystic Fibrosis
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Active IndicationsN/A
Inactive IndicationsCystic Fibrosis

Other Information

ATC CodeN/A
Related LinksN/A