FKBP12 oligonucleotide antisense therapy (Ionis Pharmaceuticals)

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Report date: 2025/03/20 14:47:55
NME

Base Information

Drug NameFKBP12 oligonucleotide antisense therapy (Ionis Pharmaceuticals)
Drug Alias NameN/A
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionFK506-binding protein 1A degraders
TargetsFK506-binding protein 1A
Therapy Area/IndicationsIron Overload
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesIonis Pharmaceuticals Inc
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsIron Overload
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A